TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Niemann-Pick disease type C

Elevation of plasma lysosphingomyelin-509 and urinary bile acid metabolite in Niemann-Pick disease type C-affected individuals - Top Articles selected by the Editor - Molecular Genetics and Metabolism Reports - Journal - Elsevier

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Niemann–Pick Disease Type C

Niemann–Pick type C Mnemonic

Main therapies and point of action in Niemann type C disease.

Terapia Génica para Niemann Pick tipo C - Grupo Teaming

Meet Parker and Woodrow, two AZ children with a rare disease

Niemann-Pick disease type C Alzheimer Society of Canada

G1 - Doença rara em menina de 2 anos mobiliza campanha de família no RS - notícias em Rio Grande do Sul